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Pre-Doc Preparatory Program (P³) in Translational Research
Do you have a rare disease research coordinator, genetic counseling assistant, or technician who may benefit from formal training in clinical and translational research?



National Survey Reveals Impact of COVID-19 on People Living with Rare Diseases and Their Families
February 16 2024


Establishing Evidence-based Guidelines for Diagnosis and Management of Liver Disease in Protoporphyrias
September 26 2023



Senior Researcher Spotlight: Mohamed Kazamel Investigates Autonomic Neuropathy in the Porphyrias
January 10 2023
